Category: Therapeutics

Cell and Gene Therapy Lesson 3: A Developing, Growing and Changing Regulatory Landscape

Cell and Gene Therapy Lesson 4: Undefined Methodologies, Unstable Technology and Potential Challenges in the GMP Regulatory Environment

Natural History Studies in Rare Diseases and Genetic Biomarkers

Patient Engagement in Clinical Trial Protocol Design and Recruitment Strategies

The Benefit of Registries for Real-World Evidence Generation in Rare Disease Research

Eligibility Criteria in Clinical Trials

The Challenges of Immuno-Oncology Combined Clinical Development, Part IV

The Challenges of Immuno-Oncology Clinical Development, Part III

The Challenges of Immuno-Oncology Clinical Development, Part II